Is FDA Breakthrough Status For TSHA-102 Reshaping The Investment Case For Taysha Gene Therapies (TSHA)?

Taysha Gene Therapies recently received FDA Breakthrough Therapy Designation for its Rett syndrome gene therapy TSHA-102, following encouraging REVEAL trial results and protocol alignment to enable a ...

Taysha Gene (TSHA) Hovers Around Its 52-Week High As It Continues to Advance Rett Syndrome Program

With strong 1-year returns and upside potential, Taysha Gene Therapies, Inc. (NASDAQ:TSHA) secures a spot on our list of the ...
Pharmaceutical Technology on MSN

FDA approves Acadia’s Daybue Stix for Rett syndrome

The US Food and Drug Administration has approved Acadia Pharmaceuticals’ Daybue Stix (trofinetide), a dye and ...
The American Journal of Managed Care

Treatment and Symptom Management for Rett Syndrome

An expert discusses the current treatment landscape of Rett syndrome including the goals of treatment and implications for utilization management strategies with the disease. David Lieberman, MD, PhD: ...
KPLC

Health Headlines: Breakthrough drug may stop progression of Rett Syndrome

ST. LOUIS, Mo. (Ivanhoe Newswire) – Imagine your toddler learning to walk and talk and then all of a sudden, your child stops and starts regressing inside of themselves. That’s what happens to ...
The American Journal of Managed Care

Insurance Authorization Considerations Associated With Rett Syndrome Treatment

Paige Nues: Many families are learning new language, such as Medicaid and the waiver system, and are getting their heads wrapped around things like Rett syndrome being on the Compassionate Allowance ...
MPR

FDA Clears New Trofinetide Formulation for Rett Syndrome Treatment

Daybue Stix, a strawberry-flavored trofinetide powder mixable with water-based liquids, gains FDA approval for Rett syndrome treatment.
Business Wire

Acadia Pharmaceuticals Submits New Drug Application to the U.S. FDA for Trofinetide for the Treatment of Rett Syndrome

SAN DIEGO--(BUSINESS WIRE)--Acadia Pharmaceuticals Inc. (Nasdaq: ACAD) today announced that the company has submitted a New Drug Application (NDA) to the U.S. Food and Drug Administration (FDA) for ...
WUNC

What you should know about Rett syndrome, the condition that Richard Engel's son had

Richard Engel, chief foreign correspondent for NBC News, announced on Thursday that his 6-year-old son Henry, diagnosed with Rett syndrome as an infant, had died. In a tweet posted on Aug. 18, Engel ...

North Texas Make-A-Wish grants a week of fun for 4-year-old boy

Thanks to the Make-A-Wish team, four-year-old Luke Chrisman and his family have been able to experience a week full of ...
KSL

Woman who dies from Rett syndrome leaves behind a legacy of love and light

This archived news story is available only for your personal, non-commercial use. Information in the story may be outdated or superseded by additional information. Reading or replaying the story in ...
People

Everything Richard Engel Said About 'Beloved' Son's Journey with Rett Syndrome Before His Death

The NBC News chief foreign correspondent announced on Twitter Thursday that his 6-year-old son Henry had died after his years-long battle with Rett Syndrome Richard Engel has long been outspoken about ...