Investor enthusiasm and evolving FDA pathways are accelerating rare disease drug development, with ultrarare conditions like ...

PHILADELPHIA (WPVI) -- February 29th is Rare Disease Day - a day aimed at spotlighting the more than 6,000 rare diseases. Many people with these ailments struggle to get a diagnosis, let alone ...

Much like the universe itself, the realm of rare diseases is constantly expanding. Unfortunately, research in the space is both timely and expensive for drugmakers who are faced with rising external ...

(WFSB) - This Saturday, hundreds of people will show compassion for and bring hope to those who are facing challenges most will never understand. The Denise D’Ascenzo Foundation Walk to Fight Rare ...

EUREKA, Mo. (First Alert 4) - A Eureka, Missouri, teen has received a place in state law. Its purpose is to raise awareness about a rare childhood disease, where most kids don’t live beyond their ...

This Rare Disease Day, observed on Feb. 28 worldwide, the American Kidney Fund is committed to improving the understanding of ...

INAUGURATION. BACK HERE IN THE METRO, COMMUNITY RALLIES AROUND SIPS ON 10TH FOR A CAUSE. THEY HELD A BAGS TOURNAMENT TO RAISE MONEY FOR RESEARCHING ZARDE. THAT STANDS FOR ZC4H2 ASSOCIATED RARE ...

(WSYR-TV) — ADTKD is a group of rare kidney disorders that can be passed down from generation to generation. and often go unnoticed Rare Kidney Disease Foundation representatives Sheri and David Dafoe ...

Khartik Uppalapati is a student at Oakton High School. He is also the founder of RareGen, a non-profit that advocates for people with rare genetic diseases. His work has won him a Princeton Prize in ...

Ashleigh McGeogh's daughter Delilah was diagnosed with Kawasaki disease, a condition that is the leading cause of acquired heart disease in UK children.

A Florida state legislator sponsored the nation's first state-backed genetic screening program after his son died from a rare genetic disease.