Through substantial leadership turnover and workforce cuts, the FDA has continued to support the advanced therapy sector, ...
ZME Science on MSN
Inside the Human Gene Editing Boom Driven by CRISPR Reshaping Everything From Medicine to Food
A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based ...
MeiraGTx is cashing in on a gene therapy that restored vision to 11 children who were born legally blind, licensing the ...
Jayden Wilsey was the first person at Boston Children's Hospital to receive human gene therapy for sickle cell disease after federal approval in 2024.
Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...
Although heart cells and skin cells contain identical instructions for creating proteins encoded in their DNA, they're able ...
Gene therapy for some diseases, including Duchenne muscular dystrophy (DMD), can be tricky because the needed gene is often too large to fit inside the viral vector used for delivery. Researchers at ...
Around the globe, heart disease remains one of the top causes of death. Once patients begin to suffer from serious heart ...
A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Other WRAL Top Stories Sickle ...
UCSF Benioff Children’s Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...
The immune system faces a delicate balancing act: it must be aggressive enough to fight infections and cancer, yet restrained ...
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